Research & Development Into Gene Therapy Standards

Time: 11:50 am
day: Day Two

Details:

  • The structural and functional complexity of CGT, along with its long-term persistence and efficacy, necessitates additional risk considerations.
  • Assessing CGT critical quality attributes (CQAs) requires the characterization of multiple parameters.
  • A unified and standardized approach to ATMP CQA assessment is essential for harmonization across the field.

Speakers: